Panel Discussion: Novel Delivery Modalities & Gene Therapy Approaches in PKD

1:50 pm - Monday 16th March 2026

  • Exploring gene therapy, antisense oligonucleotides, and CRISPR-based approaches
  • Overcoming delivery barriers to the kidney
  • Designing preclinical studies with translational relevance
  • Regulatory considerations for first-in-human studies

Speakers:

Senior Vice President & Head Of Research
Maze Therapeutics
Co- Founder & Chief Executive Officer
Estuary Biotherapeutics
Co-Founder & Chief Business Officer
Helex